Follistatin Research for Muscular Dystrophy
An evidence-based overview of research examining Follistatin in the context of muscular dystrophy. This page synthesizes findings from peer-reviewed literature.
Research Summary
In a six-person open-label Becker muscular dystrophy study, AAV1-FS344 gene transfer produced variable six-minute-walk changes. This was gene transfer, not administered native follistatin protein, and the study lacked a randomized control group. An engineered follistatin-based protein, ACE-083, increased muscle volume in a separate randomized FSHD study without consistent functional improvement.
Referenced Studies
Click any PMID to view the full study on PubMed.
Important Disclaimer
This page summarizes research findings and does not constitute medical advice. Always consult a healthcare provider before making health decisions.